We are very excited to announce our campaign to raise $2 million dollars for our Gene Therapy Program.
Angelman syndrome (AS) is a rare neurogenetic disorder, and Michelle is conquering the odds daily. A cure for Angelman syndrome is not only possible, but probable. AS has been cured in the mouse model using several different approaches. We know exactly what causes AS, and despite its often devastating effects, it is a simple disorder involving only one gene. Gene therapy has cured many diseases to date, with Angelman syndrome being a premiere candidate for a cure.
FAST is the largest non-governmental funder of Angelman syndrome research and the only organization in the world that has a detailed plan and clear path towards a cure. FAST is setting a $2 million community goal for this year. If we can meet this $2 million goal we can get those funds matched.
FAST is committed to bringing life-changing treatments to clinical trial within two years, but we need your help. We are asking everyone to join us in the Cure Angelman Now initiative because together, we CAN do this. Our time is now, and every single dollar counts in getting us closer to our goal.
As many of you know, Michelle is a beautiful girl who battles the effects of Angelman syndrome every day. She also inspires us every day with her grit and determination as well as her spontaneity and an attitude towards life and love that is a lesson for us all. She has taught us so much, and we are very grateful to have her as part of our family. We join Michelle with our determination to give her, along with so many other children with AS, the life they deserve. Please help us in this mission. Time is of the essence. Therapies and a cure are closer than ever. Join us in this fight and see miracles happen before your eyes.
Roy, Steph, Isaac, Michelle and Sary